Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...

Genetic errors can cause many different diseases, and scientists have been looking for methods to fix those errors for decades. Although many gene therapies have aimed to correct errors in individual ...

The FDA has approved Fondazione Telethon ETS’s etuvetidigene autotemcel (Waskyra) for Wiskott–Aldrich syndrome (WAS). Etuvetidigene autotemcel is the first gene therapy to be approved for this rare ...

The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...